Mr. James Watson, gene therapy is revolutionizing medicine. The fate that Watson is telling is contained in our genes and includes new technology - gene therapy. Gene therapy has revolutionized the medical world. Many physicians predict that within 20 years gene therapy may alter medical practice from treatment-based practice to preventive-based practice.
Advances in gene therapy have revolutionized our understanding of medical treatment and genetic engineering. The speed of development of these treatments is important and development of the next generation is expected to occur in several months instead of several years or decades, as in several previous treatments. Advances in these genetic technologies can affect all aspects of biotechnology from agriculture and animal care to disease. Most of today's treatments use viral vectors to transport disease resistance genes into the body. After injection, the virus adheres to the cell and releases its own genome (whole DNA group) to the nucleus and produces the necessary enzyme or protein to cure the disease. However, there are some concerns with this method. The need to mass produce viruses for therapeutic use is difficult and expensive. There is also the danger of introducing replication viruses that can harm patients already suffering from diseases.
Gene therapy is one of the biggest technical challenges in modern medicine. It is very difficult to introduce new genes into somatic cells and keep on making them alive. And there are economic problems. Can the company benefit from the development of gene therapy against rare diseases? Otherwise, who develops a cure that saves these lives and pays for that? In certain diseases, gene therapy is only effective if normal genes can be delivered to a large number of cells in the tissue (such as millions). They have to find the right cell in the appropriate organization. Once the gene reaches the site of interest, it must be activated or turned on to encode the protein. Once it is turned on it must remain on; the cell is too accustomed to shutting down genes that are active or exhibit other abnormal behaviors.